Pharma BD Deal Intelligence

Vertex Pharmaceuticals Incorporated / CRISPR Therapeutics AG

2015 · Co-Development · $2.6B · Complete

CALLED IT — OFF BY 3
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Vertex and CRISPR Therapeutics entered a strategic collaboration to use CRISPR/Cas9 gene editing for hemoglobinopathies (sickle cell disease and beta-thalassemia). This led to the development and 2023 FDA approval of Casgevy (exagamglogene autotemcel), the first CRISPR-based gene therapy approved in the US.

Key facts

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