Pharma BD Deal Intelligence

AstraZeneca PLC / Ionis Pharmaceuticals, Inc.

2021 · Licensing/Option · $4.2B · Complete

CALLED IT — OFF BY 19
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Dec 07, 2021 AstraZeneca Bullish

AstraZeneca and Ionis signed a deal to develop and commercialize eplontersen, with AstraZeneca paying $200 million upfront and up to $485 million in…

Dec 21, 2023 AstraZeneca Bullish

Wainua (eplontersen) granted first-ever regulatory approval in the US for the treatment of adults with polyneuropathy of hereditary transthyretin-mediated…

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AstraZeneca and Ionis Pharmaceuticals entered a global development and commercialization agreement for eplontersen, Ionis' LIgand-Conjugated Antisense (LICA) medicine that inhibits production of transthyretin (TTR) protein for the treatment of transthyretin amyloidosis (ATTR). Under the terms, Ionis received a $200 million upfront payment, was eligible for up to $485 million in development and approval milestones and up to $2.9 billion in sales-related milestones, plus tiered royalties ranging from low double-digit to mid-20s percent depending on region. The companies jointly develop and commercialize eplontersen in the U.S., while AstraZeneca holds exclusive rights to commercialize in the rest of the world. Hereditary ATTR amyloidosis with polyneuropathy (ATTRv-PN) was the first indication: eplontersen was approved by the U.S. FDA on December 21, 2023 under the brand name Wainua, the only ATTRv-PN treatment that can be self-administered via auto-injector. The drug is also being evaluated in the Phase 3 CARDIO-TTRansform study (>1,400 patients) for the much larger ATTR cardiomyopathy (ATTR-CM) indication, with topline data expected in the second half of 2026.

Key facts

Related deals — scored

DealYearValueOutcome
AstraZeneca PLC / Ionis Pharmaceuticals, Inc. (this deal)2021$4.2B73
AstraZeneca PLC / Daiichi Sankyo Company, Limited2019$6.9B100
AstraZeneca PLC / Alexion Pharmaceuticals Inc.2020$39.0B86
AstraZeneca PLC / Acerta Pharma2015$4.0B86
AstraZeneca PLC / Amgen Inc.2020$2.3B84
AstraZeneca PLC / MedImmune Inc.2007$15.6B82
AstraZeneca PLC / CinCor Pharma Inc.2023$1.8B78

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